FDA Hands Out Fast-Track Voucher for Kids' Rare Disease Drug
Published Date: 4/2/2026
Notice
Summary
The FDA just gave Rocket Pharmaceuticals a special priority review voucher for their rare pediatric disease treatment, KRESLADI, approved on March 26, 2026. This voucher speeds up future FDA reviews, helping get important medicines to kids with rare diseases faster. It’s a big win for patients, the company, and anyone watching rare disease breakthroughs!
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